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RNA Therapeutics Institute

  • Neil Aronin

    Neil Aronin, MD

    Academic Role: Professor

    Programs: Department of Medicine, RNA Therapeutics Institute

    Higgins Family Professor of Neuroscience
    Focus: Neurodegenerative diseases, especially Parkinson's and Huntington's diseases.
    Lab Web-page

  • Robert H. Brown, Jr.

    Robert H. Brown, Jr., MD, DPhil

    Academic Role: Professor and Vice Chair

    Programs: Department of Biochemistry and Molecular Biotechnology, Department of Neurology, RNA Therapeutics Institute

    Donna M. and Robert J. Manning Chair in Neuroscience
    Focus: Identification of gene defects in neuromuscular diseases; Amyotrophic Lateral Sclerosis

  • Fen-Biao Gao

    Fen-Biao Gao, PhD

    Academic Role: Professor

    Programs: RNA Therapeutics Institute

    The Governor Paul Cellucci Chair in Neuroscience Research
    Focus: Understanding Frontotemporal Dementia (FTD) and ALS.
    Lab Webpage

  • Guangping Gao

    Guangping Gao, PhD

    Academic Role: Professor

    Programs: Department of Microbiology, Horae Gene Therapy Center, RNA Therapeutics Institute

    Director, Horae Gene Therapy Center

    Penelope Booth Rockwell Chair in Biomedical Research
    Focus: Adeno-associated virus vectors for gene therapy of genetic diseases including Canavan Disease

  • Allan S. Jacobson

    Allan S. Jacobson, PhD

    Academic Role: Professor

    Programs: Department of Microbiology, RNA Therapeutics Institute

    Gerald L. Haidak, MD, and Zelda S. Haidak Professorship in Cell Biology (est. 1999)
    Focus: Post-transcriptional control of gene expression in model systems and genetic disorders

  • Anastasia Khvorova

    Anastasia Khvorova, PhD

    Academic Role: Professor

    Programs: Program in Molecular Medicine, RNA Therapeutics Institute

    Remondi Family Chair in Biomedical Research
    Focus: Therapeutic gene silencing in vivo.

  • Gary R. Ostroff

    Gary R. Ostroff, PhD

    Academic Role: Professor

    Programs: Program in Molecular Medicine, RNA Therapeutics Institute

    Focus: Using small to macromolecular drug delivery to phagocytes to modulate inflammation and pathologies associated with infectious, autoimmune and neurodegenerative diseases.

  • Joel Richter

    Joel Richter, PhD

    Academic Role: Professor

    Programs: Program in Molecular Medicine, RNA Therapeutics Institute

    Arthur F. Koskinas Chair in Neuroscience
    Focus: Translational control in meiosis, mitosis, and neuronal synaptic plasticity, Fragile X syndrome.

  • Dan Wang

    Dan Wang, PhD

    Academic Role: Assistant Professor

    Programs: RNA Therapeutics Institute

    Focus: AAV Gene Therapy for Genetic Diseases

  • Jonathan K. Watts

    Jonathan K. Watts, PhD

    Academic Role: Associate Professor

    Programs: RNA Therapeutics Institute

    Focus: Therapeutic gene silencing with chemically modified antisense oligonucleotides.

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